Creating the World’s First CRISPR Medicine, for Sickle Cell Disease February 20, 2025 How a genetic insight paired with gene editing technology led to a life-changing new therapy
A Universal Gene Therapy for Diamond-Blackfan Anemia Is Poised for Clinical Trials November 25, 2024 Treatment designed to work across different genetic mutations
Type 2 Diabetes in Youngsters May Be a Genetically Distinct Form of the Disorder February 23, 2024 New research challenges thinking about complex diseases with early-onset forms
